Robert Sokolic

Center for Biologics Evaluation and Research — United States

Biochemistry, Genetics and Molecular Biology · Life Sciences

26h-index3.1kcitations80works24.02yr avg
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Research Topics

Virus-based gene therapy research(33), Immunodeficiency and Autoimmune Disorders(18), CAR-T cell therapy research(15), Cell Adhesion Molecules Research(10), RNA Interference and Gene Delivery(9)

Publications78 total

Wiskott-Aldrich syndrome: a study of 577 patients defines the genotype as a biomarker for disease severity and survival
Blood·2024· 24 citedOpen Access
Severe combined immunodeficiency: improved survival leading to detection of underlying liver disease
BMC Gastroenterology·2023Open Access
Severe Combined Immunodeficiency: Improved survival leading to detection of underlying liver disease
2022Open Access
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency
New England Journal of Medicine·2021· 206 citedOpen Access
Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency
Blood·2021· 48 citedOpen Access
Selected Abstracts from the 12th Annual Meeting of the Clinical Immunology Society: 2021 Virtual Annual Meeting: Immune Deficiency and Dysregulation North American Conference
Journal of Clinical Immunology·2021· 28 citedOpen Access
The Sickle Cell Disease Multidisciplinary Clinic at the Lifespan Cancer Institute.
PubMed·2020
Lentiviral Gene Therapy with Autologous Hematopoietic Stem and Progenitor Cells (HSPCs) for the Treatment of Severe Combined Immune Deficiency Due to Adenosine Deaminase Deficiency (ADA-SCID): Results in an Expanded Cohort
Blood·2019· 14 cited
Quality of Life of Patients with Wiskott Aldrich Syndrome and X-Linked Thrombocytopenia: a Study of the Primary Immune Deficiency Consortium (PIDTC), Immune Deficiency Foundation, and the Wiskott-Aldrich Foundation
Journal of Clinical Immunology·2019· 19 citedOpen Access
Reduced Hospitalization with Establishment of a Multidisciplinary Clinic for Patients with Sickle Cell Disease
Blood·2018
A Regulatory Perspective on Cell Therapy for Cancer: Chemistry, Manufacturing and Control, and Preclinical and Clinical Considerations
2018
Gene Therapy-Based Immunotherapy Products for Human Clinical Trials: Chemistry, Manufacturing and Control, Preclinical and Clinical Considerations— An FDA Perspective
2018
Systematic Review and Decision Analysis for Current and Experimental Therapies for Wiskott-Aldrich Syndrome
Value in Health·2018
Advancing the science of patient input throughout the regulatory decision‐making process
Learning Health Systems·2017· 8 citedOpen Access
Gene therapy for the treatment of adenosine deaminase-deficient severe combined immune deficiency
Expert Opinion on Orphan Drugs·2017
Cytoreductive conditioning intensity predicts clonal diversity in ADA-SCID retroviral gene therapy patients
Blood·2017· 30 citedOpen Access
Clinical efficacy of gene-modified stem cells in adenosine deaminase–deficient immunodeficiency
Journal of Clinical Investigation·2017· 79 citedOpen Access
Wiskott-Aldrich Syndrome: A Retrospective Study on 575 Patients Analyzing the Impact of Splenectomy, Stem Cell Transplantation, or No Definitive Treatment on Frequency of Disease-Related Complications and Physician-Perceived Quality of Life
Blood·2016· 7 cited
QUALITY OF LIFE (QOL) IN PATIENTS WITH WISKOTT-ALDRICH SYNDROME (WAS)
2016 CIS Annual Meeting: Immune Deficiency & Dysregulation North American Conference·2016
Impulse oscillometry identifies peripheral airway dysfunction in children with adenosine deaminase deficiency
Orphanet Journal of Rare Diseases·2015· 10 citedOpen Access
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Frequent Co-authors

Fabio Candotti(28), Elizabeth Garabedian(19), Donald B. Kohn(14), Michael S. Hershfield(12), Alan S. Wayne(9), Kit L. Shaw(8), Alejandra Davila(8), Harry L. Malech(8), Laura M. Tuschong(8), Denise A. Carbonaro(7), Barbara C. Engel(7), Thomas R. Bauer(7), Dennis D. Hickstein(7), Chimene Kesserwan(6), Dayna Terrazas(6), Theodore B. Moore(6), Satiro De Oliveira(6), Kenneth Cornetta(6), Linda Muul(5), Sally Shupien(5)