Paula R. Clemens

Western University — Canada

Biochemistry, Genetics and Molecular Biology · Life Sciences

55h-index15.0kcitations230works5.22yr avg
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Research Topics

Muscle Physiology and Disorders(125), Virus-based gene therapy research(38), Lysosomal Storage Disorders Research(32), Glycogen Storage Diseases and Myoclonus(23), Neurogenetic and Muscular Disorders Research(22)

Publications225 total

Adrenal Suppression in Duchenne Muscular Dystrophy: Management Strategies Incorporating Novel Steroid Vamorolone
Journal of the Endocrine Society·2025Open Access
Exposure-response of serum biomarkers to vamorolone, a dissociative corticosteroidal anti-inflammatory drug, in 4- to <7-year children
Steroids·2025Open Access
Mineralocorticoid receptor antagonism of vamorolone: Evidence from LIONHEART and VISION-DMD clinical trials
Steroids·2025· 3 citedOpen Access
Test-Retest Reliability of Motor Function and Myometry Outcomes From the Vamorolone Trials in Duchenne Muscular Dystrophy
Neurology Genetics·2025· 1 citedOpen Access
Efficacy and safety of avalglucosidase alfa in patients with late-onset Pompe disease after 145 weeks of treatment during the COMET trial
Journal of Neurology·2025· 4 citedOpen Access
Some functional improvements in placebo and Delandistrogene moxeparvovec-treated trial participants explained by increased corticosteroid dosing
Journal of Neuromuscular Diseases·2025Open Access
POS1439 POLOXAMERS 188 & 182 ARE EFFECTIVE IN REPAIRING THE MEMBRANE RESEALING DEFECT IN MYOSITIS
Annals of the Rheumatic Diseases·2025Open Access
Switching Enzyme Replacement Therapy for Late‐Onset Pompe Disease From Alglucosidase Alfa to Cipaglucosidase Alfa Plus Miglustat: Post Hoc Effect Size Analysis of <scp>PROPEL</scp>
Muscle & Nerve·2025· 3 cited
Evaluating the Neurological Patient Population at the Birmingham Free Clinic, a Neurology Clinic for Uninsured Patients (P2-1.017)
Neurology·2025
Analysis of human urinary extracellular vesicles reveals disordered renal metabolism in myotonic dystrophy type 1
Nature Communications·2025· 1 citedOpen Access
Association of <i>DMD</i> Gene Variant Classes With Motor Outcomes in a Drug Registration Clinical Trial Setting
Neurology Genetics·2025· 2 citedOpen Access
Correction: Long-term safety and efficacy of cipaglucosidase alfa plus miglustat in individuals living with Pompe disease: an open-label phase I/II study (ATB200-02)
Journal of Neurology·2025Open Access
First-in-human study of epidural spinal cord stimulation in individuals with spinal muscular atrophy
Nature Medicine·2025· 15 cited
A Parent Project Muscular Dystrophy-sponsored International Workshop Report on Endocrine and Bone Issues in Patients with Duchenne Muscular Dystrophy: An Ever-changing Landscape
Journal of Neuromuscular Diseases·2025· 1 cited
A Case Study on Risk Assessment of Lane Keep Assist SW Function Using Integrated FMEA and FUSA Techniques
2024· 1 cited
Safety and efficacy of viltolarsen in ambulatory and nonambulatory males with Duchenne muscular dystrophy
Scientific Reports·2024· 7 citedOpen Access
Adrenal Suppression From Vamorolone and Prednisone in Duchenne Muscular Dystrophy: Results From the Phase 2b Clinical Trial
The Journal of Clinical Endocrinology & Metabolism·2024· 9 citedOpen Access
Assessing Pharmacogenomic <i>loci</i> Associated with the Pharmacokinetics of Vamorolone in Boys with Duchenne Muscular Dystrophy
The Journal of Clinical Pharmacology·2024· 1 citedOpen Access
Targeted Stimulation of the Sensory Afferents Improves Motoneuron Function in Humans With Spinal Muscular Atrophy
2024· 4 citedOpen Access
Return of participant-level clinical trial results to participants: pilot of a simplified centralised approach
BMJ Open·2024· 1 citedOpen Access
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Frequent Co-authors

Craig M. McDonald(21), Eric P. Hoffman(16), Erik Henricson(14), Avital Cnaan(13), Jean K. Mah(13), Yoram Nevo(13), Heather Gordish‐Dressman(12), Lauren P. Morgenroth(12), Monique M. Ryan(12), Anne M. Connolly(12), M. Tulinius(11), Richard T. Abresch(10), Richard Webster(10), Robert T. Leshner(9), Alan Pestronk(9), Tina Duong(9), Nancy L. Kuntz(9), Richard S. Finkel(8), Julaine Florence(8), John Day(8)