Melanie K. Smith

University of Pennsylvania — United States

Biochemistry, Genetics and Molecular Biology · Life Sciences

7h-index313citations9works0.02yr avg
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Research Topics

Virus-based gene therapy research(2), Diverse Aspects of Tourism Research(1), Osteoarthritis Treatment and Mechanisms(1), Cellular Mechanics and Interactions(1), Knee injuries and reconstruction techniques(1)

Publications9 total

Lipid nanoparticle-encapsulated mRNA therapy corrects serum total bilirubin level in Crigler-Najjar syndrome mouse model
Molecular Therapy — Methods & Clinical Development·2023· 11 citedOpen Access
Treating Transthyretin Amyloidosis via Adeno-Associated Virus Vector Delivery of Meganucleases
Human Gene Therapy·2022· 5 citedOpen Access
Determining the Minimally Effective Dose of a Clinical Candidate Adeno-Associated Virus Vector in a Mouse Model of Hemophilia A
Human Gene Therapy·2021· 2 citedOpen Access
Muscle-directed AAV gene therapy rescues the maple syrup urine disease phenotype in a mouse model
Molecular Genetics and Metabolism·2021· 16 cited
Increasing the Specificity of AAV-Based Gene Editing through Self-Targeting and Short-Promoter Strategies
Molecular Therapy·2020· 20 citedOpen Access
A Gene Therapy Approach to Improve Copper Metabolism and Prevent Liver Damage in a Mouse Model of Wilson Disease
Human Gene Therapy Clinical Development·2019· 23 cited
Early, focal changes in cartilage cellularity and structure following surgically induced meniscal destabilization in the mouse
Journal of Orthopaedic Research®·2016· 34 citedOpen Access
Seeing through Musculoskeletal Tissues: Improving In Situ Imaging of Bone and the Lacunar Canalicular System through Optical Clearing
PLoS ONE·2016· 55 citedOpen Access
Issues in Cultural Tourism Studies
2015· 147 cited

Frequent Co-authors

Jenny A. Greig(6), James M. Wilson(6), Elizabeth L. Buza(4), Scott N. Ashley(3), Hanying Yan(3), Joanna K Chorazeczewski(3), Michael A. David(2), Christopher Price(2), Jayme M.L. Nordin(2), Yanqing Zhu(2), Peter Bell(2), Camilo Breton(2), Thomas Furmanak(2), Matthew Jennis(2), Ian M. Berke(1), Joseph P. Miola(1), Rachael N. Pilachowski(1), Avery T. White(1), Ryan C. Locke(1), Christine Draper(1)