Dolan Sondhi

Cornell University — United States

Medicine · Health Sciences

36h-index4.9kcitations114works3.02yr avg
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Research Topics

Lysosomal Storage Disorders Research(48), Virus-based gene therapy research(43), Cytomegalovirus and herpesvirus research(11), RNA regulation and disease(10), Cellular transport and secretion(9)

Publications114 total

Prime Editing of Alzheimer’s Disease High-Risk APOE4 Allele by Brain-Directed Adeno-Associated Virus Vectors
Human Gene Therapy·2025· 1 cited
Topline results from Phase 1/2 AAV gene therapy (LX1001) in APOE4/4 homozygotes with Alzheimer’s disease
Alzheimer s & Dementia·2025Open Access
Twenty-Year Survival Analysis of Adeno-Associated Virus Vector Serotype 2-Mediated Gene Therapy to the Central Nervous System for CLN2 Disease
Human Gene Therapy·2025· 3 citedOpen Access
Advances in Gene Therapy for CLN2 (Batten) Disease
Translational Neuroscience·2025· 1 citedOpen Access
CNS Gene Therapy for APOE4 Homozygote-Associated Alzheimer’s Disease
Translational Neuroscience·2025Open Access
AAVrh.10 delivery of novel APOE2-Christchurch variant suppresses amyloid and Tau pathology in Alzheimer’s disease mice
Molecular Therapy·2024· 13 citedOpen Access
Expression and processing of mature human frataxin after gene therapy in mice
Scientific Reports·2024· 3 citedOpen Access
Expression and processing of mature human frataxin after gene therapy in mice
Research Square (Research Square)·2023Open Access
Assessment of Safety and Biodistribution of AAVrh.10hCLN2 Following Intracisternal Administration in Nonhuman Primates for the Treatment of CLN2 Batten Disease
Human Gene Therapy·2023· 9 citedOpen Access
Positron Emission Tomography Quantitative Assessment of Off-Target Whole-Body Biodistribution of I-124-Labeled Adeno-Associated Virus Capsids Administered to Cerebral Spinal Fluid
Human Gene Therapy·2023· 10 citedOpen Access
Assessment of Residual Full-Length SV40 Large T Antigen in Clinical-Grade Adeno-Associated Virus Vectors Produced in 293T Cells
Human Gene Therapy·2023· 6 citedOpen Access
Identification of Safe and Effective Intravenous Dose of AAVrh.10hFXN to Treat the Cardiac Manifestations of Friedreich's Ataxia
Human Gene Therapy·2023· 15 citedOpen Access
Safety of Intravenous Administration of an AAV8 Vector Coding for an Oxidation-Resistant Human α1-Antitrypsin for the Treatment of α1-Antitrypsin Deficiency
Human Gene Therapy·2023· 7 citedOpen Access
Long‐term functional correction of cystathionine β‐synthase deficiency in mice by adeno‐associated viral gene therapy
Journal of Inherited Metabolic Disease·2021· 14 citedOpen Access
Automated Retinal Layer Segmentation in <i>CLN2</i>-Associated Disease: Commercially Available Software Characterizing a Progressive Maculopathy
Translational Vision Science & Technology·2021· 5 citedOpen Access
Safety of Direct Intraparenchymal AAVrh.10-Mediated Central Nervous System Gene Therapy for Metachromatic Leukodystrophy
Human Gene Therapy·2020· 38 citedOpen Access
Slowing late infantile Batten disease by direct brain parenchymal administration of a rh.10 adeno-associated virus expressing <i>CLN2</i>
Science Translational Medicine·2020· 67 citedOpen Access
Cocaine vaccine dAd5GNE protects against moderate daily and high-dose “binge” cocaine use
PLoS ONE·2020· 24 citedOpen Access
Quantitative Whole-Body Imaging of I-124-Labeled Adeno-Associated Viral Vector Biodistribution in Nonhuman Primates
Human Gene Therapy·2020· 37 citedOpen Access
Stress-Induced Mouse Model of the Cardiac Manifestations of Friedreich's Ataxia Corrected by AAV-mediated Gene Therapy
Human Gene Therapy·2020· 33 cited
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Frequent Co-authors

Ronald G. Crystal(44), Stephen M. Kaminsky(30), Neil R. Hackett(19), Douglas Ballon(16), Jonathan P. Dyke(15), Bishnu P. De(14), Jonathan B. Rosenberg(13), Barry E. Kosofsky(10), Marı́a J. Chiuchiolo(10), Linda Heier(9), Mark M. Souweidane(9), Michael G. Kaplitt(9), Stefan Worgall(8), Alvin Chen(7), Odelya E. Pagovich(6), Kaleb Yohay(5), Bruce M. Greenwald(4), Sébastien Monette(4), Henning U. Voss(4), Patrick Aubourg(4)