Anna Fabiano

The San Raffaele Telethon Institute for Gene Therapy — Italy

Biochemistry, Genetics and Molecular Biology · Life Sciences

7h-index495citations14works5.62yr avg
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Research Topics

Virus-based gene therapy research(8), CRISPR and Genetic Engineering(5), Pluripotent Stem Cells Research(2), RNA Interference and Gene Delivery(2), Pancreatic function and diabetes(2)

Publications14 total

Tweaking lentiviral vector design balances efficacy and safety in liver-directed gene therapy for familial hypercholesterolemia
Molecular Therapy·2025
Spatiotemporal liver dynamics shape hepatocellular heterogeneity and impact in vivo gene engineering
Journal of Hepatology·2025· 3 citedOpen Access
In vivo haemopoietic stem cell gene therapy enabled by postnatal trafficking
Nature·2025· 9 citedOpen Access
Enhancing the potency of in vivo lentiviral vector mediated gene therapy to hepatocytes
Nature Communications·2025· 9 citedOpen Access
Identification of hepatocyte-primed cholangiocytes in the homeostatic liver by in vivo lentiviral gene transfer to mice and non-human primates
Cell Reports·2025· 3 citedOpen Access
Low-density lipoproteins receptor (LDLR) liver gene therapy normalizes LDL cholesterol (LDL-C) and prevents atherosclerosis in a familial hypercholesterolemia (FH) mouse model
Atherosclerosis·2024· 1 citedOpen Access
GP64-pseudotyped lentiviral vectors target liver endothelial cells and correct hemophilia A mice
EMBO Molecular Medicine·2024· 14 citedOpen Access
Spatio-temporal dynamics of the liver shapes hepatocytes heterogeneity and impacts in vivo gene transfer and editing
Research Square (Research Square)·2023· 1 citedOpen Access
Identification of Hepatocyte-Primed Biliary Epithelial Cells in the Homeostatic Liver by <i>in vivo</i> Lentiviral Gene Transfer to Mice and Non-Human Primates
SSRN Electronic Journal·2023Open Access
Correction of β-thalassemia by CRISPR/Cas9 editing of the α-globin locus in human hematopoietic stem cells
Blood Advances·2021· 74 citedOpen Access
Author Correction: Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins
Nature Communications·2020· 5 citedOpen Access
Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins
Nature Communications·2020· 45 citedOpen Access
IgG-cleaving endopeptidase enables in vivo gene therapy in the presence of anti-AAV neutralizing antibodies
Nature Medicine·2020· 296 citedOpen Access
Cystathionine beta-synthase c.844ins68 gene variant and non-syndromic cleft lip and palate
American Journal of Medical Genetics Part A·2005· 35 cited

Frequent Co-authors

Michela Milani(9), Alessio Cantore(9), Francesco Starinieri(8), Mauro Biffi(8), Fabio Russo(8), Francesca Sanvito(6), Monica Volpin(5), Rossana Norata(5), Eugenio Montini(5), Stefano Beretta(5), Cesare Canepari(4), Luigi Naldini(4), Cesare Canepari(4), Ivan Merelli(4), Giulia Pavani(3), Marine Laurent(3), Erika Cantelli(3), Jean‐Paul Concordet(3), Annarita Miccio(3), Mario Amendola(3)