Valérie Ferreira

UniQure (Netherlands) — Netherlands

Biochemistry, Genetics and Molecular Biology · Life Sciences

23h-index6.3kcitations41works0.02yr avg
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Research Topics

Virus-based gene therapy research(16), RNA Interference and Gene Delivery(6), Viral Infections and Immunology Research(6), NF-κB Signaling Pathways(5), CRISPR and Genetic Engineering(4)

Publications41 total

miRNA-Mediated Knockdown of ATXN3 Alleviates Molecular Disease Hallmarks in a Mouse Model for Spinocerebellar Ataxia Type 3
Nucleic Acid Therapeutics·2021· 22 citedOpen Access
Cell-Based Tracers as Trojan Horses for Image-Guided Surgery
International Journal of Molecular Sciences·2021· 10 citedOpen Access
The fiber optic gyro 'adventure' at Photonetics, iXsea and now iXblue
2020· 43 cited
Seroprevalence of Pre-Existing Nabs Against AAV1, 2, 5, 6 and 8 in South African Hemophilia B Patient Population
Blood·2019· 6 cited
Enhanced Factor IX Activity following Administration of AAV5-R338L “Padua” Factor IX versus AAV5 WT Human Factor IX in NHPs
Molecular Therapy — Methods & Clinical Development·2019· 33 citedOpen Access
Clinical Considerations for Capsid Choice in the Development of Liver-Targeted AAV-Based Gene Transfer
Molecular Therapy — Methods & Clinical Development·2019· 90 citedOpen Access
Immunoadsorption enables successful rAAV5-mediated repeated hepatic gene delivery in nonhuman primates
Blood Advances·2019· 55 citedOpen Access
Therapeutic hFIX Activity Achieved after Single AAV5-hFIX Treatment in Hemophilia B Patients and NHPs with Pre-existing Anti-AAV5 NABs
Molecular Therapy — Methods & Clinical Development·2019· 120 citedOpen Access
THU-365-Adeno-associated virus-serotype-specific transduction patterns in mice and non-human primates liver tissue: Implications for therapeutic efficacy
Journal of Hepatology·2019
THU-363-Lipid nanoparticle pre-treatment improves adeno-associated virus diffusion in the primate liver and enables an increase of therapeutic transgene expression
Journal of Hepatology·2019
Successful Repeated Hepatic Gene Delivery in Mice and Non-human Primates Achieved by Sequential Administration of AAV5 ch and AAV1
Molecular Therapy·2017· 73 citedOpen Access
700. Successful Repeated Hepatic Gene Delivery in Mice and Non-Human Primates Achieved by Sequential Administration of AAV5 and AAV1 Vector Serotypes
Molecular Therapy·2016· 1 citedOpen Access
310. Analysis of AAV5 Biodistribution and Viral Shedding in the Presence or Absence of Neutralizing Antibodies
Molecular Therapy·2016Open Access
701. Successful In Vivo Re-Administration of AAV with the Use of Two-Step AAV Injection
Molecular Therapy·2016Open Access
424. AAV Re-Administration Following Pediatric Application: Effect of Age at First Administration
Molecular Therapy·2016Open Access
Recombinant AAV Integration Is Not Associated With Hepatic Genotoxicity in Nonhuman Primates and Patients
Molecular Therapy·2016· 170 citedOpen Access
Immune Responses to AAV-Vectors, the Glybera Example from Bench to Bedside
Frontiers in Immunology·2014· 110 citedOpen Access
Immune Responses to Intramuscular Administration of Alipogene Tiparvovec (AAV1-LPL <sup>S447X</sup> ) in a Phase II Clinical Trial of Lipoprotein Lipase Deficiency Gene Therapy
Human Gene Therapy·2013· 129 citedOpen Access
Mir‐142‐3p target sequences reduce transgene‐directed immunogenicity following intramuscular adeno‐associated virus 1 vector‐mediated gene delivery
The Journal of Gene Medicine·2013· 65 cited
Murine CD4+CD25- cells activated in vitro with PMA/ionomycin and anti-CD3 acquire regulatory function and ameliorate experimental colitis in vivo
BMC Gastroenterology·2012· 12 citedOpen Access
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Frequent Co-authors

Harald Petry(17), Anna Majowicz(11), Sander van der Marel(7), S J van Deventer(6), Marie Körner(5), Gloria González‐Aseguinolaza(5), Karin L. Kwikkers(5), Sander van Deventer(5), Daniël W. Hommes(4), Nadine Tarantino(4), David Salas(4), Nerea Zabaleta(4), Hans Pannekoek(3), Hein W. Verspaget(3), Martin de Haan(3), Estefanía Rodríguez‐García(3), Lukas Schwarz(3), Anne S. De Groot(3), Carlie J.M. de Vries(2), Cornelis F.M. Sier(2)