Arnold Sengooba

Medicine · Health Sciences

3h-index47citations7works0.02yr avg
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Research Topics

Lysosomal Storage Disorders Research(3), Virus-based gene therapy research(2), Metabolism and Genetic Disorders(2), Nanoparticle-Based Drug Delivery(1), Nanoplatforms for cancer theranostics(1)

Publications7 total

Natural variations in AAVHSC16 significantly reduce liver tropism and maintain broad distribution to periphery and CNS
Molecular Therapy — Methods & Clinical Development·2022· 5 citedOpen Access
Summary of nonclinical data for gene therapy developmental candidate HMI-203 for mucopolysaccharidosis type II (MPS II, or Hunter syndrome)
Molecular Genetics and Metabolism·2022
HMI-203: Gene therapy developmental candidate for mucopolysaccharidosis type II (MPS II), or Hunter syndrome
Molecular Genetics and Metabolism·2021
HMI-203: Investigational gene therapy for mucopolysaccharidosis type II (MPS II), or Hunter syndrome
Molecular Genetics and Metabolism·2021
Sustained Correction of a Murine Model of Phenylketonuria following a Single Intravenous Administration of AAVHSC15-PAH
Molecular Therapy — Methods & Clinical Development·2020· 29 citedOpen Access
Single intravenous dose of AAVHSC15 vector with human phenylalanine hydroxylase transgene results in sustained correction of phenylketonuria in the PAH mouse model
Molecular Genetics and Metabolism·2019
Abstract 2065: Magnetic resonance imaging with an iron oxide nanoparticle demonstrates the preclinical feasibility of predicting intratumoral uptake and activity of MM-398, a nanoliposomal irinotecan (nal-IRI)
Cancer Research·2014· 13 cited

Frequent Co-authors

Deiby Faulkner(6), Albert Seymour(6), Omar L. Francone(6), Nancy Avila(5), Serena Dollive(4), Liana Behmoiras(4), Monicah Kivaa(4), Alec Tzianabos(4), Jeff L. Ellsworth(3), Kruti Patel(3), Laura J. Smith(3), Tania A. Seabrook(3), Lindsay Schulman(3), Jingyan Zhao(3), Steve Woodcock(3), Sean R. Smith(3), Jacinthe Gingras(3), Seemin Seher Ahmed(2), Hillard Rubin(2), Diana Lamppu(2)