Leszek Lisowski

National Academy of Medicine — United States

Biochemistry, Genetics and Molecular Biology · Life Sciences

32h-index4.0kcitations134works6.02yr avg
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Research Topics

Virus-based gene therapy research(74), CRISPR and Genetic Engineering(44), RNA Interference and Gene Delivery(24), Viral Infectious Diseases and Gene Expression in Insects(15), Viral Infections and Immunology Research(14)

Publications134 total

Renovating Neural Networks With Viral‐Mediated Gene Transfer From A Tissue Contacting Matrix Mimic
Small·2026Open Access
Preferential vulnerability of cortical GABAergic interneurons to <i>Nalcn</i> deficiency
2026Open Access
Expanding the Genotypic and Phenotypic Spectrum of PGAP1 Deficiency: Clinical and Functional Insights from 15 Patients
2026Open Access
Spatially precise neuron formation via hydrogel mediated modulation of the host astrocyte response
2025Open Access
AAV2 Bypasses Direct Endosomal Escape by Using AAVR to Access the Trans-Golgi Network en Route to the Nucleus
2025· 1 citedOpen Access
Wild-type and engineered adeno-associated viral vectors produce comparable opsin expression and light-evoked responses in rat skeletal muscle
Molecular Therapy — Methods & Clinical Development·2025· 1 citedOpen Access
Highly Efficient Functional Editing of the Native Ornithine Transcarbamylase Locus by Targeted Integration with Phenotype Correction and Restoration of Physiological Patterns of Gene Expression
2025Open Access
High-throughput evaluation of cardiac-specific promoters for adeno-associated virus mediated cardiac gene therapy
Gene Therapy·2025· 2 citedOpen Access
Genotypic, functional, and phenotypic characterization in CTNNB1 neurodevelopmental syndrome
Human Genetics and Genomics Advances·2025· 3 citedOpen Access
Maturation of human cardiac organoids enables complex disease modeling and drug discovery
Nature Cardiovascular Research·2025· 12 citedOpen Access
07-8: ENGINEERING ISLETS FOR TOLERANCE WITH PROTECTIVE GENES: UPDATE ON A FIRST IN HUMAN SAFETY STUDY WITH BABS-AAV2-A20
Transplantation·2025
Critical impact of lysine 136 in TDP-43 phase separation, compartmentalization, and aggregation in living vertebrates
iScience·2025· 2 citedOpen Access
Impact of liver fibrosis on AAV-mediated gene transfer to mouse hepatocytes
Nature Communications·2025· 6 citedOpen Access
AAV Genome Topology Decides ITR Secondary Structure
BioEssays·2025Open Access
Paving the way toward treatment solutions for CTNNB1 syndrome: a patient organization perspective
Therapeutic Advances in Rare Disease·2025· 3 citedOpen Access
Tailoring capsid-directed evolution technology for improved AAV-mediated CAR-T generation
Molecular Therapy·2024· 4 cited
Characterization of RNA editing and gene therapy with a compact CRISPR-Cas13 in the retina
Proceedings of the National Academy of Sciences·2024· 14 citedOpen Access
Alzheimer’s disease induced neurons bearing PSEN1 mutations exhibit reduced excitability
Frontiers in Cellular Neuroscience·2024· 7 citedOpen Access
AAVolve: Concatenated long-read deep sequencing enables whole capsid tracking during shuffled AAV library selection
Molecular Therapy — Methods & Clinical Development·2024· 2 citedOpen Access
O049 Maintaining long-term functional optogenetic stimulation for OSA therapy in a rodent model
SLEEP Advances·2024Open Access
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Frequent Co-authors

Ian E. Alexander(20), Mark A. Kay(12), Marti Cabanes‐Creus(12), Erhua Zhu(11), Sophia H.Y. Liao(9), Renina Gale Navarro(9), Adrian J. Thrasher(9), Adrian Westhaus(8), Anais K. Amaya(6), Grober Baltazar(6), Giorgia Santilli(6), Suzanne Scott(6), Yue Zhang(5), Sharon C. Cunningham(5), Markus Grompe(5), Michel Sadelain(5), Claus V. Hallwirth(5), Samantha L. Ginn(5), Matthieu Drouyer(5), Kimberley L. Dilworth(5)